Stem cell transplant can rectify infrequent genetic disorder in youths

Scripps Research Institute scientists have offered new hope for parents whose children suffer from the rare genetic disorder ‘cystinosis’ by showing through an experiment on mice that stem cell transplantation can successfully correct the defect (…)

In the study, the researchers used bone marrow stem cell transplantation to address symptoms of cystinosis in a mouse model (…)

In the new study, the researchers found that transplanted bone marrow stem cells carrying the normal lysosomal cystine transporter gene abundantly engrafted into every tissue of the experimental mice (…)

“The results really surprised and encouraged us. Because the defect is present in every cell of the body, we did not expect a bone marrow stem cell transplant to be so widespread and effective,” says Cherqui.
Cherqui said that adult bone marrow stem cell therapy is particularly well suited as a potential treatment for cystinosis because these cells target all types of tissues.

In addition, stem cells reside in the bone marrow for the duration of a patient’’s life, becoming active as needed, a particular benefit for a progressive disease like cystinosis. The study has been published in the journal Blood.

from http://www.newkerala.com/nkfullnews-1-114380.html

Reblog this post [with Zemanta]

Maybe you can find something interesting in the following sponsored links:

Related pages on the web
  • Baby Development Stages in Week 3 Fertilization occurs at what is perceived as the third week of pregnancy, and this is when the baby development stages really begin. Fertilization is the process that occurs when a sperm and an egg connect, forming a single cell which...
  • Virus shown to cause obesity Researchers now have proof that a virus may be involved in human obesity, according to a paper just published in the International Journal of Obesity. A virus had been shown to cause obesity in animal subjects, but the link between...
  • Male Bass in Numerous US Rivers Seem to Have Been Feminized According to Study Government scientists are figuring that one out of every five black bass in the American river basins, despite being male, have egg cells that are growing inside of their typical sex organs, and this is a sign of just how...
  • Unhooking the Obesity-Diabetes Connection Unhooking the Obesity-Diabetes Connection Understanding the link may someday lead to a cure, studies suggest By Amanda Gardner HealthDay Reporter SUNDAY, July 26 (HealthDay News) -- Scientists may be closer to solving a medical mystery with huge implications for personal...
  • Bone-building drugs linked to heart arrhythmia Fosamax from Merck and Reclast, a bone-fortifying drug from Novartis AG, have been linked to atrial fibrillation in studies of their use to treat post-menopausal women for osteoporosis. Reclast, which is administered in a once-yearly intravenous infusion, showed slightly greater...
Blog Traffic Exchange Related articles on this site

0 Responses to “Stem cell transplant can rectify infrequent genetic disorder in youths”


  1. No Comments

Leave a Reply




Related Posts Widget for Blogs by LinkWithin